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Ultragenyx Pharmaceutical Inc.

SectorHealth CareIndustryBiotechnology: Pharmaceutical PreparationsIPO2014
$21.42-0.49 (-2.24%)
News25/Ratings12

Ultragenyx Pharmaceutical Inc., a biopharmaceutical company, focuses on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in the United States. Its biologic products include Crysvita (burosumab), an antibody targeting fibroblast growth factor 23 for the treatment of X-linked hypophosphatemia, as well as tumor-induced osteomalacia; Mepsevii, an enzyme replacement therapy for the treatment of children and adults with Mucopolysaccharidosis VII; and Dojolvi for treating long-chain fatty acid oxidation disorders. The company is also developing DTX401, an adeno-associated virus 8 (AAV8) gene therapy clinical candidate for the treatment of patients with glycogen storage disease type Ia; DTX301, an AAV8 gene therapy product candidate for the treatment of patients with ornithine transcarbamylase; UX143, a human monoclonal antibody for the treatment of osteogenesis imperfecta; GTX-102, an antisense oligonucleotide for the treatment of Angelman syndrome; UX701, for the treatment of Wilson disease; and UX053 for the treatment of glycogen storage disease type III. Ultragenyx Pharmaceutical Inc. has collaboration and license agreement with Kyowa Kirin Co., Ltd.; Saint Louis University; Baylor Research Institute; REGENXBIO Inc.; Bayer; GeneTx; Mereo; University of Pennsylvania; Arcturus Therapeutics Holdings Inc., Solid Biosciences Inc.; and Daiichi Sankyo Co., Ltd. Ultragenyx Pharmaceutical Inc. was incorporated in 2010 and is headquartered in Novato, California.

Price$21.42-0.37 (-1.70%)
01:30 PM07:30 PM
News · 26 weeks74-35%
2025-12-14: 12025-12-21: 02025-12-28: 52026-01-04: 22026-01-11: 22026-01-18: 12026-01-25: 22026-02-01: 52026-02-08: 22026-02-15: 22026-02-22: 32026-03-01: 82026-03-08: 32026-03-15: 12026-03-22: 42026-03-29: 52026-04-05: 02026-04-12: 02026-04-19: 92026-04-26: 22026-05-03: 52026-05-10: 12026-05-17: 92026-05-24: 02026-05-31: 22026-06-07: 0
2025-12-142026-06-07
Mix4190d
  • Insider20(49%)
  • Other10(24%)
  • SEC Filings8(20%)
  • Earnings2(5%)
  • Analyst1(2%)

Latest news

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RARE FAQ

7 questions
  • What does Ultragenyx Pharmaceutical Inc. do?
    Ultragenyx Pharmaceutical Inc., a biopharmaceutical company, focuses on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in the United States. Its biologic products include Crysvita (burosumab), an antibody targeting fibroblast growth factor 23 for the treatment of X-linked hypophosphatemia, as well as tumor-induced osteomalacia; Mepsevii, an enzyme replacement therapy for the treatment of children and adults with Mucopolysaccharidosis VII; and Dojolvi for treating long-chain fatty acid oxidation...
  • Where does RARE stock trade?
    Ultragenyx Pharmaceutical Inc. (RARE) is listed on NASDAQ.
  • What sector and industry is RARE in?
    Ultragenyx Pharmaceutical Inc. operates in the Health Care sector, Biotechnology: Pharmaceutical Preparations industry.
  • When did Ultragenyx Pharmaceutical Inc. go public?
    Ultragenyx Pharmaceutical Inc. (RARE) completed its IPO in 2014.
  • What are analysts saying about RARE?
    Ultragenyx Pharmaceutical Inc. has had 8 recent analyst actions on file. The most recent action was from Goldman: Neutral with a $2500.00 price target on 2026-03-24. Recent price targets cluster around $2500.00.
  • What companies are similar to RARE?
    Notable peers in the same industry include LLY (Eli Lilly and Company), AZN (AstraZeneca PLC), JNJ (Johnson & Johnson), ABBV (AbbVie Inc.), MRK (Merck & Company Inc.). Compare RARE side-by-side with any of them on Quantisnow.
  • How can I track RARE on Quantisnow?
    Quantisnow aggregates Ultragenyx Pharmaceutical Inc.'s SEC filings, analyst ratings, insider transactions, FDA approvals, and press releases the moment they hit the wire (Wall Street's wire, on your screen.). Follow RARE to receive live email and push alerts on every new disclosure.